Gene therapy for Dravet Syndrome: Evaluation of adenoviral vectors expressing SCN1A in a new mouse model
Dravet Syndrome (DS) is a severe encephalopathy with infantile onset, characterized by seizures refractory to conventional antiepileptic drugs, increased risk of sudden unexpected death in epilepsy (SUDEP), as well as cognitive, behavioral and motor comorbidities. The vast majority of DS cases are c...
| Main Authors: | , , |
|---|---|
| Format: | info:eu-repo/semantics/doctoralThesis |
| Language: | eng |
| Published: |
Universidad de Navarra
2021
|
| Subjects: | |
| Online Access: | https://hdl.handle.net/10171/61043 |