Development of disease and drug models for rare diseases: Application to Acute Intermittent Porphyria.

This thesis illustrates an evolving mechanistic framework developed for Acute Intermittent Porphyria (AIP) at the discovery and pre-clinical stages of development. This type of approach provides quantitative support for already established mechanisms of the biological system involved, allows the sea...

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Bibliographic Details
Main Authors: Vera-Yunca, D. (Diego), Troconiz, I.F. (Iñaki F.), Parra-Guillen, Z.P. (Zinnia Patricia)
Format: info:eu-repo/semantics/doctoralThesis
Language:eng
Published: Universidad de Navarra 2022
Subjects:
Online Access:https://hdl.handle.net/10171/62717