Development of disease and drug models for rare diseases: Application to Acute Intermittent Porphyria.
This thesis illustrates an evolving mechanistic framework developed for Acute Intermittent Porphyria (AIP) at the discovery and pre-clinical stages of development. This type of approach provides quantitative support for already established mechanisms of the biological system involved, allows the sea...
Main Authors: | Vera-Yunca, D. (Diego), Troconiz, I.F. (Iñaki F.), Parra-Guillen, Z.P. (Zinnia Patricia) |
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Format: | info:eu-repo/semantics/doctoralThesis |
Language: | eng |
Published: |
Universidad de Navarra
2022
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Subjects: | |
Online Access: | https://hdl.handle.net/10171/62717 |
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